Matching articles for "cerebral folate deficiency"
Leucovorin for Cerebral Folate Deficiency
The Medical Letter on Drugs and Therapeutics • May 11, 2026; (Issue 1754)
The FDA has approved use of oral leucovorin calcium (folinic
acid) for treatment of cerebral folate transport deficiency in
patients who have a confirmed variant in the folate receptor 1
gene (FOLR1-CFTD)....
The FDA has approved use of oral leucovorin calcium (folinic
acid) for treatment of cerebral folate transport deficiency in
patients who have a confirmed variant in the folate receptor 1
gene (FOLR1-CFTD). It is the first drug to be approved for this
extremely rare disorder.